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Recent Market Movements Highlight Top Gainers
Financial Modeling Prep· 2025-10-01 22:00
公司股价表现 - Palisade Bio Inc (PALI) 股价大幅上涨83.77%至1.57美元 成交量达143,677,281股 [1] - Ouster Inc (OUSTZ) 股价上涨76.55%至0.09美元 成交量为150,580股 [2] - Ryvyl Inc (RVYL) 股价跃升72.64%至0.511美元 成交量高达231,813,941股 [3] - Klotho Neurosciences Inc (KLTOW) 股价上涨50.11%至0.14美元 成交量为134,508股 [4] 公司特定事件与业务 - Palisade Bio 宣布扩大承销公开发行 以每股0.70美元发行1.71亿股 筹集1.2亿美元资金 用于推进治疗自身免疫、炎症和纤维化疾病的新型疗法 [1] - Ouster 是一家高分辨率激光雷达传感器供应商 其技术服务于汽车、工业、机器人和智能基础设施等行业 [2] - Ryvyl Inc 前身为GreenBox POS 专注于基于区块链的支付解决方案 在软件基础设施领域展现潜力 [3] - Klotho Neurosciences 致力于开发针对关键健康问题的基因疗法产品 其肌萎缩侧索硬化疗法KLTO-202获得美国FDA孤儿药认定 [4] 行业与市场动态 - 股价大幅上涨的公司反映了行业的多样性 涵盖生物技术、医疗保健、技术和金融服务等领域 [5]
uniQure N.V. (QURE) Reports Positive Phase I/II Results, Prepares FDA BLA Submission
Yahoo Finance· 2025-09-30 16:46
We recently compiled a list of the 12 Best Performing Healthcare Stocks to Buy Right Now. uniQure N.V. is one of them. uniQure N.V. (NASDAQ:QURE) is a leading gene therapy company focused on developing transformative treatments for severe medical conditions. Its pipeline includes HEMGENIX for hemophilia B and AMT-130, a gene therapy candidate for Huntington’s disease, which has recently attracted significant attention. In late September 2025, uniQure N.V. (NASDAQ:QURE) announced positive topline results ...
4D Molecular Therapeutics: This Gene Therapy Company May Soon Surprise Investors (NASDAQ:FDMT)
Seeking Alpha· 2025-09-30 09:08
4D Molecular Therapeutics (NASDAQ: FDMT ) seems an attractive buy in late 2025, especially for long-term investors with a high-risk appetite and who can tolerate short-term volatility. With shares priced at $8.35 (as of September 29) and a market capitalizationI am an MBA in finance and an engineering graduate. I have also completed the CFA certification.I am involved in international trade and have been passionately tracking global equity markets for more than 7 years. I mainly focus on spotting long-term ...
4D Molecular Therapeutics: This Gene Therapy Company May Soon Surprise Investors
Seeking Alpha· 2025-09-30 09:08
公司投资价值 - 4D Molecular Therapeutics (FDMT) 在2025年末对能承受短期波动和高风险的长期投资者而言似乎是一个有吸引力的买入机会 [1] - 公司股价为8.35美元(截至9月29日) [1] 作者背景 - 文章作者拥有金融MBA和工程学学士学位,并已完成CFA认证 [1] - 作者从事国际贸易,并热情追踪全球股市超过7年 [1] - 作者主要专注于在生物技术、制药、医院和医疗设备领域发现长期价值投资 [1] - 在过去两年中,作者也开始研究大麻和工业大麻领域 [1]
Candel trial shows promise for gene therapy in prostate cancer
Proactiveinvestors NA· 2025-09-29 12:20
About this content About Ian Lyall Ian Lyall, a seasoned journalist and editor, brings over three decades of experience to his role as Managing Editor at Proactive. Overseeing Proactive's editorial and broadcast operations across six offices on three continents, Ian is responsible for quality control, editorial policy, and content production. He directs the creation of 50,000 pieces of real-time news, feature articles, and filmed interviews annually. Prior to Proactive, Ian helped lead the business outpu ...
源自诺贝尔奖技术:亨廷顿舞蹈症的首次基因治疗,成功缓解疾病进程
生物世界· 2025-09-28 04:05
亨廷顿病 ( Huntington's disease ) ,也称为 亨廷顿舞蹈症 ,是一种罕见的遗传性神经退行性疾病,会 导致大脑中神经细胞的逐渐退化,从而造成身体能力、运动、思维和精神障碍的损伤。目前的治疗方法只 能控制症状,而无法改变或缓解疾病进程 。 一种一次性 基因疗法 能够显著减缓 亨廷顿病 的病情发展,或许为治疗这种 罕见的遗传性神经退行性疾病 开辟了首个能够改变疾病进程的疗法。 在一项针对 29 名处于亨廷顿病早期衰退阶段患者的试验中,接受高剂量基因疗法直接注入大脑的患者,其 疾病进展在三年内减缓了 75% ,而对照组则没有这种效果 。 这是首次真正证实了亨廷顿病的疾病进程可 以被减缓 。 这促使亨廷顿病的研究人员畅想未来——这种致命遗传病有望成为可治疗的疾病。 撰文丨王聪 编辑丨王多鱼 排版丨水成文 基因治疗公司 uniQure 本周发布的数据显示,该疗法在多项临床指标上均具有显著的统计学意义,接受该 疗法的患者脊髓液中与神经退行性病变有关的有毒蛋白质水平有所降低。基于这些发现,uniQure 公司表 示,他们计划明年为该疗法申请监管批准。 患有亨廷病的人通常会发现自己的症状逐年加重,他们一 ...
Benzinga Bulls And Bears: Oracle, Costco, NIO — And Wall Street Snaps Its Slide Benzinga Bulls And Bears: Oracle, Costco, NIO — And Wall Street Snaps Its Slide
Benzinga· 2025-09-27 12:04
市场整体表现 - 美国三大股指结束三日连跌 标普500上涨约0.6% 道指上涨约299点 纳斯达克上涨约0.4% [1] - 美国第二季度GDP终值达3.8% 超出预期 8月PCE通胀同比升至2.7% 核心PCE维持在2.9% [2] - 黄金价格突破3800美元/盎司 年内涨幅达43% 白银单月上涨约15% [2] 美联储政策动向 - 美联储主席鲍威尔强调货币政策"无预设路径" 反映通胀粘性与劳动力市场降温迹象之间的政策张力 [3] - 市场关注后续PCE数据、就业数据及美联储对进一步宽松预期的应对策略 [3] 看涨个股表现 - 甲骨文公司因成为TikTok美国安全运营及云服务提供商 股价在延长交易时段跳涨 [4] - UniQure公司宣布亨廷顿病基因疗法试验结果后单日暴涨248% 斯提费尔及莱林克公司分别将目标价上调至65美元和68美元 [5] - 好市多第四季度营收达861.6亿美元超预期 调整后EPS为5.87美元 同店销售额同比增长5.7% 会员费收入跃升至17.2亿美元 [6] 看跌个股表现 - 比特币跌破110,000美元 以太坊跌破3,900美元 XRP跌破2.75美元 导致Riot Platforms、MARA Holdings、HIVE Digital Technologies、Coinbase Global及Strategy Inc等加密货币关联股票大幅下挫 [7] - 北京要求自2026年1月1日起电动汽车出口需获得新许可 蔚来汽车和理想汽车股价应声下跌 [8] - 自由港麦克莫兰公司因印尼Grasberg矿难被Scotiabank从行业表现优异下调至行业表现 目标价从55美元降至45美元 预计2026年产量下降35% 2025-2026年收益/EBITDA/自由现金流大幅削减 [9][10]
uniQure Announces Pricing of Upsized $300 Million Public Offering
Globenewswire· 2025-09-26 03:38
LEXINGTON, Mass. and AMSTERDAM, Sept. 25, 2025 (GLOBE NEWSWIRE) -- uniQure N.V. (Nasdaq: QURE), a leading gene therapy company advancing transformative therapies for patients with severe medical needs, today announced the pricing of its previously announced underwritten public offering of 5,789,473 ordinary shares at a public offering price of $47.50 per share, and, in lieu of ordinary shares to certain investors, pre-funded warrants to purchase 526,316 of its ordinary shares at the public offering price pe ...
UniQure: How QURE Stock Rises 10x To $500?
Forbes· 2025-09-25 10:20
CANADA - 2025/09/24: In this photo illustration, the uniQure logo is seen displayed on a smartphone screen. (Photo Illustration by Thomas Fuller/SOPA Images/LightRocket via Getty Images)SOPA Images/LightRocket via Getty ImagesUniQure announced groundbreaking results for AMT-130, its gene therapy targeting Huntington's disease, showing a statistically significant 75% reduction in disease progression in a pivotal Phase I/II trial. ((UniQure's Press Release, Sep 24, 2025)) This milestone marks the first therap ...
Market Highlights: Significant Gains in Stocks and ETFs
Financial Modeling Prep· 2025-09-24 22:00
公司股价表现 - uniQure N V股价飙升至45.1美元 单日涨幅达230.16% 年高低点分别为51.19美元和4.45美元 成交量58,563,496股远超日均114万股的交易水平 [2] - SHF Holdings股价跃升至7.01美元 单日涨幅达115.03% 日高触及9.18美元 成交量29,808,900股显著高于日均851,200股的交易规模 [3] - Nushares ETF Trust旗下三只ETF价格均实现100%增长 NHYB收报25.01美元 NSCI收报25.03美元 NXUS收报25.02美元 均呈现交易量激增现象 [4] 公司重大进展 - uniQure实验性基因疗法成功治疗亨廷顿病 该突破性进展直接推动股价单日涨幅超240% [2][6] - SHF Holdings推出行业首个全托管大麻银行计划 为金融机构提供全面运营与合规外包服务 该创新金融服务推动股价大幅上涨 [3] 金融产品特征 - Nuveen高收益公司债券ETF提供高收益公司债多元化投资 exposure [4] - 证券化收入ETF聚焦证券化收入资产投资领域 [4] - Nuveen国际综合债券ETF覆盖国际综合债券投资标的 [4]